Trial

NCT04925960

Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG
Phase IIITERMINATEDEFFICACY/FUTILITYConfidence: HIGH
Sponsor
Maggie's Pearl, LLC
Collaborators
Condition
Pmm2-CDG
Intervention
Epalrestat
Why stopped
Due to futility
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2025-09-25