Trial
NCT04771416
Study of Safety, Tolerability and Efficacy of PBKR03 in Pediatric Subjects With Early Infantile Krabbe Disease
Phase ISUSPENDEDOPERATIONALConfidence: HIGH
Sponsor
Gemma Biotherapeutics
Collaborators
—
Condition
Leukodystrophy, Globoid Cell
Intervention
PBKR03
Why stopped
The study was stopped due to changes in the company strategy.
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2026-06-30