Trial
NCT04708314
An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy
Phase IVTERMINATEDOTHER/UNKNOWNConfidence: LOW
Sponsor
Rare Disease Research, LLC
Collaborators
Sarepta Therapeutics, Inc.
Condition
Duchenne Muscular Dystrophy
Intervention
Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53]
Why stopped
The Sponsor has decided to focus their resources on other areas of therapy.
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2026-04-03