Trial
NCT04679389
Acetazolamide Efficacy in Ataxia in PMM2-CDG
Phase IITERMINATEDOPERATIONALConfidence: HIGH
Sponsor
Mayo Clinic
Collaborators
Seattle Children's Hospital; Children's Hospital of Philadelphia
Condition
Pmm2-CDG
Intervention
Placebo
Why stopped
Lack of funding
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2025-03-20