Trial

NCT04041232

PBA Use for Treatment of ATF6-/- Patients
Early Phase ISUSPENDEDOPERATIONALConfidence: HIGH
Sponsor
Columbia University
Collaborators
Condition
ACHROMATOPSIA 7
Intervention
PBA
Why stopped
Administrative changes
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2025-09-12