Trial
NCT02456103
Extension Study of Ataluren in Participants With Nonsense Mutation Cystic Fibrosis
Phase IIITERMINATEDEFFICACY/FUTILITYConfidence: MEDIUM
Sponsor
PTC Therapeutics
Collaborators
—
Condition
Cystic Fibrosis
Intervention
Ataluren
Why stopped
Cystic Fibrosis (CF) data from the double-blind CF Study PTC124-GD-021-CF did not meet endpoints.
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2020-04-27