Trial

NCT02357225

A Pilot Study of Pyridostigmine in Pompe Disease
Early Phase ITERMINATEDEFFICACY/FUTILITYConfidence: MEDIUM
Sponsor
University of Florida
Collaborators
Condition
Pompe Disease
Intervention
Pyridostigmine Bromide
Why stopped
The drug was ineffective in improving function in Pompe's disease
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2018-05-15