Trial

NCT02193867

Clinical Study In Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency
Phase IITERMINATEDOTHER/UNKNOWNConfidence: LOW
Sponsor
Alexion Pharmaceuticals, Inc.
Collaborators
Condition
Lysosomal Acid Lipase Deficiency
Intervention
Sebelipase Alfa
Why stopped
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2019-11-18