Trial
NCT02030015
Synergistic Enteral Regimen for Treatment of the Gangliosidoses
Phase IVTERMINATEDOTHER/UNKNOWNConfidence: LOW
Sponsor
University of Minnesota
Collaborators
Rare Diseases Clinical Research Network; National Center for Advancing Translational Sciences (NCATS); National Institute of Neurological Disorders and Stroke (NINDS); National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Lysosomal Disease Network
Condition
GM1 Gangliosidoses
Intervention
miglustat
Why stopped
Efficacy
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2021-04-14