Trial

NCT01512888

Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants
Phase ISUSPENDEDOTHER/UNKNOWNConfidence: LOW
Sponsor
St. Jude Children's Research Hospital
Collaborators
National Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California Institute for Regenerative Medicine (CIRM)
Condition
Severe Combined Immunodeficiency Disease, X-linked
Intervention
CL20-i4-EF1α-hγc-OPT
Why stopped
voluntary hold
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2025-11-10