Trial
NCT01331018
Gene Therapy for Fanconi Anemia
Phase ITERMINATEDOPERATIONALConfidence: HIGH
Sponsor
Fred Hutchinson Cancer Center
Collaborators
National Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma Limited
Condition
Fanconi Anemia
Intervention
Bone Marrow Aspiration
Why stopped
Study ended early due to end of funding.
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2024-05-17