Trial
NCT01299727
Extension of Study HGT-SAN-055 Evaluating Administration of rhHNS in Patients With Sanfilippo Syndrome Type A (MPS IIIA)
Phase ITERMINATEDOTHER/UNKNOWNConfidence: LOW
Sponsor
Shire
Collaborators
—
Condition
Sanfilippo Syndrome
Intervention
rhHNS-10 mg
Why stopped
Completion of follow-up period
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2021-06-14