Trial
NCT00935753
Trial of Kuvan in Lesch-Nyhan Disease
Phase IIWITHDRAWNOTHER/UNKNOWNConfidence: LOW
Sponsor
University of California, San Diego
Collaborators
BioMarin Pharmaceutical
Condition
Behavioral Manifestations of Lesch-Nyhan Disease
Intervention
sapropterin
Why stopped
Contractual issues
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2019-08-02