Trial
NCT00681811
Open-Label Extension Study of Recombinant Human Arylsulfatase A (HGT-1111) in Late Infantile MLD
Phase IITERMINATEDEFFICACY/FUTILITYConfidence: MEDIUM
Sponsor
Shire
Collaborators
—
Condition
Late Infantile Metachromatic Leukodystrophy
Intervention
HGT-1111
Why stopped
Terminated prior to planned completion date due to lack of efficacy.
Provenance
Dataset: 2026-07-02 • Source: ClinicalTrials.gov API v2 • Last update: 2021-06-08